Regeneron says it will offer the new gene therapy free of charge to the small pool of eligible patients. Ilhan Omar's family winery shut down after Congress demands answers Iran escalates Hormuz ...
The treatment, the first of its kind, was approved by the Food and Drug Administration on Thursday. “Our baby was born deaf, and now he can hear,” said one parent. By Gina Kolata The Food and Drug ...
The US Food and Drug Administration on Thursday approved the first gene therapy for inherited hearing loss, a one-time treatment that proved to be life-changing for a small number of children in a ...
USA Rare Earth announced plans to buy Brazilian rare earths miner Serra Verde in a deal worth $2.8 billion. Rare earths have come to the fore as a key bargaining chip in the ongoing geopolitical ...
SAN FRANCISCO (KGO) -- Ten-year-old Oli and his family have spent much of his young life searching for the missing piece of a puzzle: a treatment for a debilitating form of childhood epilepsy known as ...
The 'Imperfect Women' actress shares her kids with husband Nnamdi Asomugha Kayla Grant is a writer-reporter at PEOPLE. She has been working at PEOPLE since 2025. Her work has previously appeared in ...
Charles and Curtshandra Duplechain’s two daughters, Jade and Ivory, have been diagnosed with Infantile Neuroaxonal Dystrophy, or INAD Two Louisiana parents are raising awareness for INAD, a rare ...
CONCORD, N.C. — For Sadie Rae Haywood and her mother, time together isn’t just precious — it’s disappearing. Sadie is living with Sanfilippo Syndrome, a rare inherited condition that progressively ...
Children with the rare but serious allergic disease FPIES have an atypical gut microbiota compared to healthy children. This is shown in a new study from Umeå University, published in the journal the ...
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Families of children with Sanfilippo syndrome push FDA to speed rare-disease treatment approvals
Doctors say newborn screening and gene therapy access could change outcomes for children diagnosed with the disorder. Iran responds to Trump's threat of blowing up the whole country Tori Spelling and ...
Ever since her 15-year-old son Cole was diagnosed with a rare, progressive illness called Hunter syndrome when he was 2, Kim Stephens has been waiting. Waiting to see if Cole will lose his ability to ...
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