Gemma Biotherapeutics ("GEMMABio"), a clinical‑stage, global, genetic medicines company, today announced the presentation of preclinical data supporting candidate declaration for GB703, a novel, ...

Spinal muscular atrophy is a rare, genetic condition that causes progressive muscle weakness and loss of movement, and can ...

Key signs of spinal muscular atrophy include severe muscle weakness, difficulty breathing or swallowing, and missing developmental milestones.

MEDICINES for babies with spinal muscular atrophy will be funded by the NHS for all patients for the first time. Little Mix ...

What is SMA? Key signs to look out for in babies as Jesy Nelson highlights life-changing condition - Pop star Jesy Nelson has campaigned for screening to be rolled out after her twins were diagnosed w ...

Medicines watchdog approves two treatments for patients with spinal muscular atrophy ...

The decision marks a significant milestone after both medicines were previously made available through managed access agreements while additional evidence on their effectiveness was gathered. SMA is a ...

Hundreds more children with muscle-wasting condition spinal muscular atrophy (SMA) are to be offered potentially ...

Pop star Jesy Nelson has backed calls for routine screening, as Oxford University launches a study to help infants with ...

SMA is a genetic condition which causes severe muscle weakness and can affect breathing, swallowing and movement. | ITV National News ...

‘Life-changing’ SMA treatments approved for use across the NHS - ...

Treatment for a rare muscle-wasting condition for a nine-year-old has "fundamentally changed the course of his life", his ...