PPT1 is a recombinant protein used to treat an ultra-rare disease called Batten disease CLN1 for which there is ...
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What Is Batten Disease? All About The Fatal Genetic Conditions Causing Waste Build Up In Kids Brain
A life-saving medicine for children with Batten disease, a rare and fatal genetic disorder, is set to be pulled from the market because of unresolved pricing negotiations. Otherwise called CLN2, ...
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