FIREFISH Part 2 study met its primary endpoint by demonstrating a significant increase in motor milestones in infants aged 1-7 months after 12 months of treatment Large, pivotal global study confirms ...
Spinal muscular atrophy (SMA) is a rare genetic condition that causes progressive muscle weakness, which, when untreated, prevents infants with the most severe form from gaining motor development - ...
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Scholar Rock’s Phase 2 Study on Apitegromab: A Potential Game-Changer for SMA Treatment
Scholar Rock Holding (($SRRK)) announced an update on their ongoing clinical study. Scholar Rock Holding (SRRK) is currently conducting a Phase 2, ...
The study is designed as a cohort observational model with a prospective time perspective. Participants are followed throughout their pregnancy and up to 12 weeks postpartum, while their babies are ...
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