Huntington's disease (HD) has long been impossible to cure, but new research is finally giving fresh hope. HD is a ...
TAMPA, Fla. (WFLA) — For the first time, scientists have successfully treated someone suffering from Huntington’s disease, a fatal genetic illness with no cure. The Mayo Clinic reports that the ...
Families with Huntington’s need this to be true more than most. The devastating neurodegenerative disease is caused by a CAG ...
UCL and uniQure report the first treatment to slow Huntington’s disease with gene therapy AMT-130. High-dose patients had 75% less progression over three years compared with standard care. uniQure ...
"I am absolutely thrilled and excited that we now have a potential treatment for this truly devastating disorder and what the data means is that for a person who has Huntington's disease, they will be ...
NEW YORK, Sept. 25, 2025 /PRNewswire/ -- The Hereditary Disease Foundation (HDF) is proud to announce its new name, Huntington's Disease Foundation, with the same unwavering commitment to fund ...
uniQure reported positive topline data from the pivotal Phase I/II study of AMT-130 for the treatment of Huntington’s disease. The study met its prespecified primary endpoint, with high-dose AMT-130 ...
ST. LOUIS — Scientists may have reached a breakthrough in the fight against Huntington’s disease, a rare and fatal inherited brain disorder with no cure. For the first time, a gene therapy has been ...
Shares of UniQure were higher after the gene therapy company said it had scheduled a Type A meeting with the Food and Drug Administration to discuss a Biologics License Application for the company's ...
Researchers at the University of Leeds and Lancaster University in the UK have identified a new potential target for the treatment of Alzheimer's disease—PDE4B. Their work is published in ...